Skip to main content
NACFC 2026 Main banner
Icon Legend
This session is not in your schedule.
This session is in your schedule. Click again to remove it.
Presentation Icons
Recorded Session
Recorded Session
Livestreamed Session
Livestreamed Session
Session is Ticketed (Add-on Session through Registration)
Session is Ticketed (Add-on Session through Registration)
Food Available for Session Attendees
Food Available for Session Attendees
Session includes an in person invitee/speaker with CF
Session includes an in person invitee/speaker with CF

Workshop

PTAC/CFTR

W29-- Alternative Therapeutic Targets for CF

Friday, October 9, 2026
10:15 AM - 12:15 PM EDT

Presentation Order:



1. Suppression of CFTR Nonsense Mutations by Distinct Classes of Small Molecule Readthrough Agents – Presented by David Bedwell

2. Specific Potentiation of the TMEM16A Chloride Channel Can Rescue Impaired Mucociliary Transport in Human Airway Models of Cystic Fibrosis – Presented by Peihang Li

3. A Novel Gamma-Secretase Inhibitor Reprograms Maladaptive Cystic Fibrosis Airway Epithelia and Restores Mucociliary Clearance – Presented by Marcos Milla

4. SPL23, an Exon-Skipping Antisense Oligonucleotide for PwCF Carrying the W1282X Variant – Presented by Efrat Ozeri-Galai

5. A Randomized 28-Day, Double-Blind Cross-Over Study to Evaluate the Safety, Efficacy & Pharmacokinetics of ETD001, an Inhaled ENaC Blocker, in People with Cystic Fibrosis – Presented by Marcus A. Mall